Advance therapies for rare diseases
Utmost rare pattern still warrant authorized treatments despite major advances in disquisition and furnishing the tools to understand their molecular base. Remedial modalities for restating advances in rare complaint knowledge into implicit medicines are known as orphan drugs. With this in mind, also are the advance antidotes, including small molecules, monoclonal antibodies, protein relief antidotes, oligonucleotides and gene and cell antidotes, as well as drug repurposing. For each system, we consider its strengths and manacle as a platform for rare complaint remedy expansion and describe clinical progress so far in developing drugs predicated on it. We also bat named overarching pattern in the expansion of antidotes for rare conditions, analogous as engagement of cases in the process and digital tools.
Related Conference of Advance therapies for rare diseases
October 30-31, 2025
20th World Conference on Infectious Diseases, Prevention and Control
Paris, France
December 11-12, 2025
8th Annual Congress on Bacterial, Viral and Infectious Diseases
Prague, Czech Republic
December 17-18, 2025
17th Global Conference on Nephrology and Infectious Diseases
Amsterdam, Netherlands
December 22-23, 2025
6th International Conference on Microbiology and Infectious Diseases
Barcelona, Spain
January 20-21, 2026
7th Annual Meeting on Infectious Diseases, Microbiology & Beneficial Microbes
Aix-en-Provence, France
January 22-23, 2026
10th International Conference on Infectious Diseases: Control and Prevention
Aberdeen, UK
May 14-15, 2026
13th International Conference on Infectious Diseases, Bacteriology and Antibiotics
Paris, France
May 18-18, 2026
6th World Congress on Tuberculosis, Lung Infections, and Respiratory Care
Aix-en-Provence, France
Advance therapies for rare diseases Conference Speakers
Recommended Sessions
- Adrenal
- Advance therapies for rare diseases
- Disorders of Calcium & Phosphate Homeostasis
- Genetic disorders of Glucose & Insulin Homeostasis
- Genetic Endocrine Tumour Syndromes
- Growth & Genetic Obesity Syndromes
- Hypothalamic and Pituitary Conditions
- Immunological Rare Diseases
- Infectious Diseases
- Orphan Drugs
- Rare Autoimmune Diseases
- Thyroid
Related Journals
Are you interested in
- A prospective study of dermatological infections - Emerging Infectious Diseases 2025 (Canada)
- Advancements in Vaccines and Therapeutic - Infectious Diseases 2026 (France)
- AI in Diagnostic Microbiology and Genomics - Infectious Meet 2025 (Spain)
- AI-Powered Predictive Outbreak Analytics - Infectious Meet 2025 (Spain)
- Antigen-Antibody Reactions - Infectious Diseases 2026 (France)
- Antimicrobial Drugs - Infectious Meet 2025 (Spain)
- Antimicrobial Resistance - Emerging Infectious Diseases 2025 (Canada)
- Antimicrobial Resistance (AMR) - Infection Congress 2026 (UK)
- Antimicrobial Stewardship/Antimicrobial Resistance - Infection Prevention 2026 (Spain)
- Bacterial Infections and Antimicrobial Resistance (AMR) - Euro Infectious Diseases 2026 (UK)
- Bacterial Infections and Diseases - Infectious Diseases 2026 (France)
- Bacterial Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Bacterial, Parasitic and Fungal Infections - Infection Prevention 2026 (Spain)
- Biofertilizers - Infectious Diseases 2026 (France)
- Biomarkers for Rare Disease Diagnosis and Treatment - Rare Diseases Congress 2026 (Czech Republic)
- Biomedical Research - Rare Diseases Congress 2026 (Czech Republic)
- Blood Borne Infections/Sepsis/Septicaemia - Infection Prevention 2026 (Spain)
- Cardiovascular Diseases and Disorders - Emerging Infectious Diseases 2025 (Canada)
- Causes and Symptoms of Infections - Infection Prevention 2026 (Spain)
- Causes and Symptoms of Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Challenges of Living with a Rare Disease: - Rare Diseases Congress 2026 (Czech Republic)
- Changing Patterns of Infectious Diseases - Emerging Infectious Diseases 2025 (Canada)
- Climate Change and Infectious Diseases - Infection Congress 2026 (UK)
- Climate Change, Urbanization, and Infectious Disease Spread - Euro Infectious Diseases 2026 (UK)
- Clinical and Case Reports - INFECTIOUS DISEASES-2026 (France)
- Clinical Case Reports and Case Studies - Rare Diseases Congress 2026 (Czech Republic)
- Clinical Management of Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Clinical Research on Orphan Drugs - Rare Diseases Congress 2026 (Czech Republic)
- Clinical Trials and Novel Therapeutics - Infectious Meet 2025 (Spain)
- Coronavirus Disease (COVID-19) - INFECTIOUS DISEASES-2026 (France)
- COVID-19 - Infectious Diseases 2026 (France)
- COVID-19 Variants - Infection Congress 2026 (UK)
- Covid_19 Infections - Infection Prevention 2026 (Spain)
- Dental diseases & Infections - Emerging Infectious Diseases 2025 (Canada)
- Diabetes and Wound Care - Emerging Infectious Diseases 2025 (Canada)
- Diagnosis f infectious Diseases - Infection Prevention 2026 (Spain)
- Diagnostics and Laboratory Techniques - Emerging Infectious Diseases 2025 (Canada)
- Diagnostics and Molecular Tools in Infectious Disease - Euro Infectious Diseases 2026 (UK)
- Diagnostics, Microbiology, and Laboratory Science - Infectious Meet 2025 (Spain)
- Diarrheal Diseases - Infectious Meet 2025 (Spain)
- Different Types of Rare Diseases: - Rare Diseases Congress 2026 (Czech Republic)
- Drug Discovery for Rare Diseases: - Rare Diseases Congress 2026 (Czech Republic)
- Emerging and Re-Emerging Infections - Infection Prevention 2026 (Spain)
- Emerging and Re-emerging Infectious Diseases - Infectious Meet 2025 (Spain)
- Emerging Infectious Diseases - Infection Congress 2026 (UK)
- Emerging Technologies in Rare Disease Research - Rare Diseases Congress 2026 (Czech Republic)
- Epidemiology - INFECTIOUS DISEASES-2026 (France)
- Epidemiology - Infection Prevention 2026 (Spain)
- Epidemiology and Public Health - Infection Congress 2026 (UK)
- Epidemiology and Surveillance - Emerging Infectious Diseases 2025 (Canada)
- Food Pathology - Infectious Meet 2025 (Spain)
- Fungal Infections - Infectious Diseases 2026 (France)
- Fungal Infections: Diagnosis and Emerging Threats - Euro Infectious Diseases 2026 (UK)
- Fungal Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Gastrointestinal and Urinary Tract Infections - Infection Prevention 2026 (Spain)
- Gene Expression - Infectious Diseases 2026 (France)
- Global Climatic Change and Emerging Infectious Diseases - Emerging Infectious Diseases 2025 (Canada)
- Global Health Security - Emerging Infectious Diseases 2025 (Canada)
- Global Health Security - Infection Congress 2026 (UK)
- Global hotspots and correlates of emerging zoonotic diseases - Emerging Infectious Diseases 2025 (Canada)
- Global Trends in Emerging Infections - Infection Prevention 2026 (Spain)
- Health Economics and Market Access for Orphan Drugs - Rare Diseases Congress 2026 (Czech Republic)
- Healthcare-Associated Infections (HAIs) and Antimicrobial Stewardship - Infectious Meet 2025 (Spain)
- Hepatitis Prevention - Infection Prevention 2026 (Spain)
- Herpes Simplex Virus - Infectious Meet 2025 (Spain)
- HIV/AIDS and Sexually Transmitted Infections (STIs) - Euro Infectious Diseases 2026 (UK)
- Hospital-Acquired Infections (Nosocomial Infections) - Infection Congress 2026 (UK)
- Human Monkeypox: An Emerging Zoonosis - Emerging Infectious Diseases 2025 (Canada)
- Immunizations and Vaccination - Infection Prevention 2026 (Spain)
- Infection Control and Hospital-Acquired Infections (HAIs) - Euro Infectious Diseases 2026 (UK)
- Infection Control in Critical Care - Infection Prevention 2026 (Spain)
- Infection Control Procedures - Infection Prevention 2026 (Spain)
- Infection Prevention and Control - Infection Prevention 2026 (Spain)
- Infection Prevention and Control (IPC) - Infection Congress 2026 (UK)
- Infection, Immunity and Inflammation - INFECTIOUS DISEASES-2026 (France)
- Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Infectious Diseases and Cancer - Infectious Diseases 2026 (France)
- Infectious Diseases and Immune Deficiencies - Rare Diseases Congress 2026 (Czech Republic)
- Infectious Diseases Epidemiology - INFECTIOUS DISEASES-2026 (France)
- Infectious Diseases Prevention, Control and Cure - INFECTIOUS DISEASES-2026 (France)
- Internal Medicine for Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Introduction and Causes of New Rare Diseases: - Rare Diseases Congress 2026 (Czech Republic)
- Molecular Diagnosis of Infectious Diseases - Infectious Meet 2025 (Spain)
- Mutations - Infectious Diseases 2026 (France)
- Neuro Infections - Infection Prevention 2026 (Spain)
- Neuro Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Nosocomial Infections & Control - INFECTIOUS DISEASES-2026 (France)
- Nosocomial Infections and Control - Infection Prevention 2026 (Spain)
- Nosocomial Infections and Their Control Strategies - Emerging Infectious Diseases 2025 (Canada)
- One Health and Emerging Global Threats - Euro Infectious Diseases 2026 (UK)
- One Health and Zoonoses - Infectious Meet 2025 (Spain)
- One Health Approach - Infection Congress 2026 (UK)
- Ophthalmological Infections - Infection Prevention 2026 (Spain)
- Orphan Drugs Potentiality - Rare Diseases Congress 2026 (Czech Republic)
- Outbreak Investigation and Response - Emerging Infectious Diseases 2025 (Canada)
- Pandemic Preparedness - Infection Congress 2026 (UK)
- Parasitic Infections - Infectious Diseases 2026 (France)
- Parasitic Infections and Neglected Tropical Diseases (NTDs) - Euro Infectious Diseases 2026 (UK)
- Parasitology & Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Pediatric Infectious Diseases - Emerging Infectious Diseases 2025 (Canada)
- Pediatric Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Pediatric Infectious Diseases - Infection Prevention 2026 (Spain)
- Pediatric Infectious Diseases and Immunization Programs - Euro Infectious Diseases 2026 (UK)
- Perspectives on Gastrointestinal Infections - Emerging Infectious Diseases 2025 (Canada)
- Pharmacology of Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Plants Diseases and Infection Control - Infection Prevention 2026 (Spain)
- Prion Diseases - Infectious Diseases 2026 (France)
- Probiotics and Prebiotics - Infectious Diseases 2026 (France)
- Probiotics and Prebiotics - Infectious Diseases 2026 (France)
- Public Health Policy and Preparedness - Emerging Infectious Diseases 2025 (Canada)
- Rapid Diagnostic Technologies - Infection Congress 2026 (UK)
- Rare Autoimmune Disorders: - Rare Diseases Congress 2026 (Czech Republic)
- Rare Bone Diseases - Rare Diseases Congress 2026 (Czech Republic)
- Rare Cancer - Rare Diseases Congress 2026 (Czech Republic)
- Rare Diseases and Orphan Drugs: - Rare Diseases Congress 2026 (Czech Republic)
- Rare Infectious Diseases - Infection Prevention 2026 (Spain)
- Rare Nutritional and Metabolic Diseases - Rare Diseases Congress 2026 (Czech Republic)
- Rare Skin Diseases - Rare Diseases Congress 2026 (Czech Republic)
- Research on Medicine and Vaccine for Covid-19 - INFECTIOUS DISEASES-2026 (France)
- Respiratory Infections - Infectious Meet 2025 (Spain)
- Respiratory Infectious Diseases and Therapy - Infection Prevention 2026 (Spain)
- Respiratory Tract Infections: Viral and Bacterial Perspectives - Euro Infectious Diseases 2026 (UK)
- SARS and MERS: Recent Insights into Emerging Coronaviruses - Emerging Infectious Diseases 2025 (Canada)
- Sepsis and Critical Infections in Clinical Practice - Euro Infectious Diseases 2026 (UK)
- Sexually Transmitted Diseases - Infection Prevention 2026 (Spain)
- Sexually Transmitted Diseases (STDs) and Infections (STIs) - Infectious Diseases 2026 (France)
- Sexually Transmitted Infections (STIs) and Blood-Borne Viruses - Infectious Meet 2025 (Spain)
- Social Behavior on Infectious Diseases - Infectious Meet 2025 (Spain)
- Surgical Site Infections - Infection Prevention 2026 (Spain)
- The Science of SARS-CoV-2 - Emerging Infectious Diseases 2025 (Canada)
- Therapeutics and Clinical Management - Infectious Meet 2025 (Spain)
- Therapeutics and Treatment Strategies - Emerging Infectious Diseases 2025 (Canada)
- Tropical diseases - Infection Prevention 2026 (Spain)
- Tropical Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Tuberculosis - Infectious Meet 2025 (Spain)
- Tuberculosis and Mycobacterial Diseases - Euro Infectious Diseases 2026 (UK)
- Vaccine Development - Infection Congress 2026 (UK)
- Vaccine Research and Development - Euro Infectious Diseases 2026 (UK)
- Vaccines and Immunization - Emerging Infectious Diseases 2025 (Canada)
- Vaccines and Vaccination - INFECTIOUS DISEASES-2026 (France)
- Vaccines and Vaccination for Rare Diseases: - Rare Diseases Congress 2026 (Czech Republic)
- Vaccinology and Immunization - Infectious Meet 2025 (Spain)
- Vector-Borne and Parasitic Diseases - Infectious Meet 2025 (Spain)
- Vector-Borne Diseases - Infection Congress 2026 (UK)
- Vector-borne diseases: New Approaches to Control Vector from disease transmission - Emerging Infectious Diseases 2025 (Canada)
- Veterinary Diseases - INFECTIOUS DISEASES-2026 (France)
- Veterinary Diseases - Infection Prevention 2026 (Spain)
- Veterinary Infectious Diseases - Infectious Diseases 2026 (France)
- Viral Hepatitis - Infectious Meet 2025 (Spain)
- Viral Infections and Diseases - Infectious Diseases 2026 (France)
- Viral Infections and Outbreaks - Infection Congress 2026 (UK)
- Viral Infections and Recent Advancements - Infection Prevention 2026 (Spain)
- Viral Infections: Trends, Variants, and Global Impact - Euro Infectious Diseases 2026 (UK)
- Viral Infectious Diseases - INFECTIOUS DISEASES-2026 (France)
- Zoonotic and Vector-Borne Diseases - Euro Infectious Diseases 2026 (UK)
- Zoonotic Diseases - Infection Congress 2026 (UK)